<description>&lt;p&gt;In this episode, Dr. Paloma Giangrande, Editor-in-Chief of Molecular Therapy Nucleic Acids, speaks with Normand Allaire, Head of Genomics at the Cystic Fibrosis Foundation Therapeutics Lab. They discuss the article, Upregulation of a CFTR mRNA isoform has therapeutic potential for the treatment of 3&amp;rsquo; CFTR PTC variants, which introduces an ASO-based therapeutic approach to cystic fibrosis for the 10% of patients who lack an approved treatment.&lt;/p&gt; &lt;p&gt;&lt;strong&gt;Music:&lt;/strong&gt;&amp;nbsp;'Electric Dreams' by Scott Buckley - released under CC-BY 4.0.&amp;nbsp;&lt;a href="https://www.scottbuckley.com.au/"&gt;www.scottbuckley.com.au&lt;/a&gt;&lt;/p&gt;&lt;p&gt;&lt;a href="https://asgct.org/membership/donate" rel="payment"&gt;Show your support for ASGCT!: https://asgct.org/membership/donate&lt;/a&gt;&lt;/p&gt;&lt;p&gt;See &lt;a href="https://omnystudio.com/listener"&gt;omnystudio.com/listener&lt;/a&gt; for privacy information.&lt;/p&gt;</description>

ASGCT Podcast Network

American Society of Gene & Cell Therapy

A CFTR mRNA isoform for the treatment of 3’ CFTR PTC variants with Normand Allaire

MAY 21, 202640 MIN
ASGCT Podcast Network

A CFTR mRNA isoform for the treatment of 3’ CFTR PTC variants with Normand Allaire

MAY 21, 202640 MIN

Description

In this episode, Dr. Paloma Giangrande, Editor-in-Chief of Molecular Therapy Nucleic Acids, speaks with Normand Allaire, Head of Genomics at the Cystic Fibrosis Foundation Therapeutics Lab. They discuss the article, Upregulation of a CFTR mRNA isoform has therapeutic potential for the treatment of 3’ CFTR PTC variants, which introduces an ASO-based therapeutic approach to cystic fibrosis for the 10% of patients who lack an approved treatment. Music: 'Electric Dreams' by Scott Buckley - released under CC-BY 4.0. www.scottbuckley.com.auShow your support for ASGCT!: https://asgct.org/membership/donateSee omnystudio.com/listener for privacy information.